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Messenger RNA rescues medium-chain acyl-CoA dehydrogenase deficiency in fibroblasts from patients and a murine model

  • Xue Jun Zhao
  • , Ai Walid Mohsen
  • , Stephanie Mihalik
  • , Keaton Solo
  • , Shakuntala Basu
  • , Ermal Aliu
  • , Huifang Shi
  • , Catherine Kochersberger
  • , Anuradha Karunanidhi
  • , Clinton Van't Land
  • , Kimberly A. Coughlan
  • , Summar Siddiqui
  • , Lisa M. Rice
  • , Shawn Hillier
  • , Eleonora Guadagnin
  • , Christine Deantonis
  • , Paloma H. Giangrande
  • , Paolo G.V. Martini
  • , Jerry Vockley

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Immunology and Microbiology

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