Synthetic mRNA rescues very long-chain acyl-CoA dehydrogenase deficiency in patient fibroblasts and a murine model
- Xue Jun Zhao
- , AI Walid Mohsen
- , Stephanie Mihalik
- , Keaton Solo
- , Ermal Aliu
- , Huifang Shi
- , Shakuntala Basu
- , Catherine Kochersperger
- , Clinton Van't Land
- , Anuradha Karunanidhi
- , Kimberly A. Coughlan
- , Summar Siddiqui
- , Lisa M. Rice
- , Shawn Hillier
- , Eleonora Guadagnin
- , Paloma H. Giangrande
- , Paolo G.V. Martini
- , Jerry Vockley
Research output: Contribution to journal › Article › peer-review
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